Leadiant Biosciences, Inc., is a U.S. research-based pharmaceutical company that dedicates considerable scientific and financial resources to the research, development, and distribution of novel and effective therapies to address the needs of people living with rare diseases.

Chiesi manufactures Revcovi, the only recombinant adenosine deaminase (ADA) approved to treat ADA-SCID in the U.S.

With Rare Resolve, X4 is delivering progress for patients by developing and commercializing innovative therapies for those with rare diseases of the immune system and significant unmet needs.

We are a global, science-led biopharmaceutical business and our innovative medicines are used by millions of patients worldwide.

Accredo is a specialty pharmacy that serves patients with complex and chronic health conditions, including cancer, hepatitis C, HIV, bleeding disorders and multiple sclerosis.

Amgen harnesses the best of biology and technology to fight the world’s toughest diseases, and make people’s lives easier, fuller and longer. We discover, develop, manufacture and deliver innovative medicines to help millions of patients.

Amgen Rare Disease also offers free dihydrorhodamine (DHR) testing for CGD through ARUP Laboratories.