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thumbnail for the ChronicXTwenties podcast which features three circles of Immune Deficiency Foundation colors, and the text "young adulthood, rare disease, and the joy you deserve".

ChronicXTwenties: Demystifying advocacy

July 17, 2025

BioCryst

Takhzyro

Plasma kallikrein inhibitor (monoclonal antibody)
Approved to prevent attacks of Hereditary Angioedema (HAE) in adult and pediatric patients 2 years and older.

Report side effects/adverse events at 1-800-FDA-1088.

Package insert

Orladeyo

Plasma kallikrein inhibitor
Approved to prevent attacks of Hereditary Angioedema (HAE) in adults and pediatric patients 12 years and older.

Report side effects/adverse events at 1-800-FDA-1088.

Package insert

Kalbitor

Plasma kallikrein inhibitor
Approved to treat acute attacks of Hereditary Angioedema (HAE) in patients 12 years and older.

Report side effects/adverse events at 1-800-FDA-1088.

Package insert

Firazyr

Bradykinin B2 receptor antagonist
Approved to treat acute attacks of Hereditary Angioedema (HAE) in adults 18 years and older.

Report side effects/adverse events at 1-800-FDA-1088.

Package insert

Andembry

Activated Factor XII (FXIIa) inhibitor (monoclonal antibody)  
Approved to prevent attacks of Hereditary Angioedema (HAE) in adult and pediatric patients aged 12 years and older.

Report side effects/adverse events at 1-866-915-6958.

Package insert

Berinert

C1 Esterase Inhibitor (Human) 
Approved to treat acute abdominal or facial or laryngeal attacks of Hereditary Angioedema (HAE) in adult and adolescent patients.

Report side effects/adverse events at 1-866-915-6958.

Package insert

Haegarda

C1 Esterase Inhibitor (Human) 
Approved to treat Hereditary Angioedema (HAE) attacks in adolescent and adult patients.

Report side effects/adverse events at 1-866-915-6958.

Package insert

Ruconest

C1 Esterase Inhibitor (Recombinant) 
Approved to treat acute attacks in adult and adolescent patients with Hereditary Angioedema (HAE).

Report side effects/adverse events at 1-800-508-0024.

Package insert
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